Israeli doctors perform world's first gene therapy for rare WWOX genetic disorder in infant

The therapy addresses a previously fatal genetic disorder affecting infants, offering hope to families facing this devastating condition.

In a hospital in Israel, a team of physicians crossed a threshold that medicine had never before reached — administering the world's first gene therapy for WWOX deficiency, a rare and historically fatal disorder that fills an infant's earliest months with unrelenting seizures. Where no treatment had existed, they chose to restore what was missing at the genetic level, delivering a functional copy of the WWOX gene directly into the cells of a developing brain. The act was at once a precise scientific intervention and a profound human gesture toward a family for whom no other door remained open.

Israeli doctors perform world's first gene therapy for rare WWOX genetic disorder in infant

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